|Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy|
GP Gao, MR Alvira, L Wang, R Calcedo, J Johnston, JM Wilson
Proceedings of the National Academy of Sciences 99 (18), 11854-11859, 2002
|Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer|
SE Raper, N Chirmule, FS Lee, NA Wivel, A Bagg, G Gao, JM Wilson, ...
Molecular genetics and metabolism 80 (1-2), 148-158, 2003
|Clades of Adeno-associated viruses are widely disseminated in human tissues|
G Gao, LH Vandenberghe, MR Alvira, Y Lu, R Calcedo, X Zhou, ...
Journal of virology 78 (12), 6381-6388, 2004
|Transduction with recombinant adeno-associated virus for gene therapy is limited by leading-strand synthesis.|
KJ Fisher, GP Gao, MD Weitzman, R DeMatteo, JF Burda, JM Wilson
Journal of virology 70 (1), 520-532, 1996
|Gene therapy vectors based on adeno-associated virus type 1|
W Xiao, N Chirmule, SC Berta, B McCullough, G Gao, JM Wilson
Journal of virology 73 (5), 3994-4003, 1999
|Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo|
H Yin, CQ Song, JR Dorkin, LJ Zhu, Y Li, Q Wu, A Park, J Yang, S Suresh, ...
Nature biotechnology 34 (3), 328-333, 2016
|Worldwide epidemiology of neutralizing antibodies to adeno-associated viruses|
R Calcedo, LH Vandenberghe, G Gao, J Lin, JM Wilson
The Journal of infectious diseases 199 (3), 381-390, 2009
|New recombinant serotypes of AAV vectors|
G Gao, LH Vandenberghe, JM Wilson
Current gene therapy 5 (3), 285-297, 2005
|Biology of adenovirus vectors with E1 and E4 deletions for liver-directed gene therapy.|
G Gao, Y Yang, JM Wilson
Journal of virology 70 (12), 8934-8943, 1996
|Acute cytokine response to systemic adenoviral vectors in mice is mediated by dendritic cells and macrophages|
Y Zhang, N Chirmule, G Gao, R Qian, M Croyle, B Joshi, J Tazelaar, ...
Molecular Therapy 3 (5), 697-707, 2001
|A Pilot Study of In Vivo Liver-Directed Gene Transfer with an Adenoviral Vector in Partial Ornithine Transcarbamylase Deficiency|
SE Raper, M Yudkoff, N Chirmule, GP Gao, F Nunes, ZJ Haskal, EE Furth, ...
Human gene therapy 13 (1), 163-175, 2002
|Isolation of highly infectious and pure adeno-associated virus type 2 vectors with a single-step gravity-flow column|
A Auricchio, M Hildinger, E O'Connor, GP Gao, JM Wilson
Human gene therapy 12 (1), 71-76, 2001
|Activation of innate immunity in nonhuman primates following intraportal administration of adenoviral vectors|
MA Schnell, Y Zhang, J Tazelaar, G Gao, QC Yu, R Qian, SJ Chen, ...
Molecular Therapy 3 (5), 708-722, 2001
|Adeno-associated viruses undergo substantial evolution in primates during natural infections|
G Gao, MR Alvira, S Somanathan, Y Lu, LH Vandenberghe, JJ Rux, ...
Proceedings of the National Academy of Sciences 100 (10), 6081-6086, 2003
|Sequestration of adenoviral vector by Kupffer cells leads to a nonlinear dose response of transduction in liver|
N Tao, GP Gao, M Parr, J Johnston, T Baradet, JM Wilson, J Barsoum, ...
Molecular Therapy 3 (1), 28-35, 2001
|Regulated delivery of therapeutic proteins after in vivo somatic cell gene transfer|
X Ye, VM Rivera, P Zoltick, F Cerasoli, MA Schnell, G Gao, JV Hughes, ...
Science 283 (5398), 88-91, 1999
|Long-term pharmacologically regulated expression of erythropoietin in primates following AAV-mediated gene transfer|
VM Rivera, G Gao, RL Grant, MA Schnell, PW Zoltick, LW Rozamus, ...
Blood 105 (4), 1424-1430, 2005
|Replication-defective vector based on a chimpanzee adenovirus|
SF Farina, G Gao, ZQ Xiang, JJ Rux, RM Burnett, MR Alvira, J Marsh, ...
Journal of virology 75 (23), 11603-11613, 2001
|Adeno-associated virus (AAV) serotype 9 provides global cardiac gene transfer superior to AAV1, AAV6, AAV7, and AAV8 in the mouse and rat|
LT Bish, K Morine, MM Sleeper, J Sanmiguel, D Wu, G Gao, JM Wilson, ...
Human gene therapy 19 (12), 1359-1368, 2008
|Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina|
J Bennett, AM Maguire, AV Cideciyan, M Schnell, E Glover, V Anand, ...
Proceedings of the National Academy of Sciences 96 (17), 9920-9925, 1999