Safety, efficacy, and tolerability of efgartigimod in patients with generalised myasthenia gravis (ADAPT): a multicentre, randomised, placebo-controlled, phase 3 trial JF Howard, V Bril, T Vu, C Karam, S Peric, T Margania, H Murai, ... The Lancet Neurology 20 (7), 526-536, 2021 | 279 | 2021 |
Pompe disease: literature review and case series M Dasouki, O Jawdat, O Almadhoun, M Pasnoor, AL McVey, ... Neurologic clinics 32 (3), 751-776, 2014 | 159 | 2014 |
A randomized trial of mexiletine in ALS: Safety and effects on muscle cramps and progression MD Weiss, EA Macklin, Z Simmons, AS Knox, DJ Greenblatt, N Atassi, ... Neurology 86 (16), 1474-1481, 2016 | 98 | 2016 |
Amyotrophic lateral sclerosis regional variants (brachial amyotrophic diplegia, leg amyotrophic diplegia, and isolated bulbar amyotrophic lateral sclerosis) O Jawdat, JM Statland, RJ Barohn, JS Katz, MM Dimachkie Neurologic clinics 33 (4), 775-785, 2015 | 58 | 2015 |
Rare variants in SQSTM1 and VCP genes and risk of sporadic inclusion body myositis Q Gang, C Bettencourt, PM Machado, S Brady, JL Holton, AM Pittman, ... Neurobiology of aging 47, 218. e1-218. e9, 2016 | 54 | 2016 |
Adaptive platform trials to transform amyotrophic lateral sclerosis therapy development S Paganoni, JD Berry, M Quintana, E Macklin, BR Saville, MA Detry, ... Annals of neurology 91 (2), 165-175, 2022 | 50 | 2022 |
Patient assisted intervention for neuropathy: comparison of treatment in real life situations (PAIN-CONTRoLS): Bayesian adaptive comparative effectiveness randomized trial RJ Barohn, B Gajewski, M Pasnoor, A Brown, LL Herbelin, KS Kimminau, ... JAMA neurology 78 (1), 68-76, 2021 | 30 | 2021 |
A Bayesian comparative effectiveness trial in action: developing a platform for multisite study adaptive randomization AR Brown, BJ Gajewski, LS Aaronson, DP Mudaranthakam, SL Hunt, ... Trials 17, 1-9, 2016 | 25 | 2016 |
Primary lateral sclerosis (PLS) functional rating scale: PLS‐specific clinimetric scale H Mitsumoto, C Chiuzan, M Gilmore, Y Zhang, Z Simmons, S Paganoni, ... Muscle & nerve 61 (2), 163-172, 2020 | 19 | 2020 |
Using automated electronic medical record data extraction to model ALS survival and progression AG Karanevich, LJ Weisbrod, O Jawdat, RJ Barohn, BJ Gajewski, J He, ... BMC neurology 18, 1-7, 2018 | 18 | 2018 |
An instrumented timed up and go in facioscapulohumeral muscular dystrophy J Huisinga, A Bruetsch, A Mccalley, M Currence, L Herbelin, O Jawdat, ... Muscle & nerve 57 (3), 503-506, 2018 | 14 | 2018 |
Investigation of the psychometric properties of the inclusion body myositis functional rating scale with rasch analysis G Ramdharry, J Morrow, S Hudgens, I Skorupinska, K Gwathmey, ... Muscle & Nerve 60 (2), 161-168, 2019 | 12 | 2019 |
Oxaloacetate treatment preserves motor function in SOD1G93A mice and normalizes select neuroinflammation-related parameters in the spinal cord SK Tungtur, HM Wilkins, RS Rogers, Y Badawi, JM Sage, A Agbas, ... Scientific reports 11 (1), 11051, 2021 | 9 | 2021 |
Use of capillary electrophoresis immunoassay to search for potential biomarkers of amyotrophic lateral sclerosis in human platelets JM Sage, LS Hall, A McVey, RJ Barohn, JM Statland, O Jawdat, ... JoVE (Journal of Visualized Experiments), e60638, 2020 | 8 | 2020 |
Satisfactory response with achieving maintenance low-dose prednisone in generalized myasthenia gravis AR Abuzinadah, D Jabari, O Jawdat, M Pasnoor, M Glenn, L Herbelin, ... Journal of clinical neuromuscular disease 20 (2), 49-59, 2018 | 8 | 2018 |
Less is more in diabetic neuropathy diagnosis: comparison of quantitative sudomotor axon reflex and skin biopsy AR Abuzinadah, P Kluding, D Wright, L D'Silva, J Ryals, B Hendry, ... Journal of clinical neuromuscular disease 19 (1), 5-11, 2017 | 7 | 2017 |
A novel physiologic marker of bulbar motor involvement in amyotrophic lateral sclerosis: Jaw muscle synergy P Rong, O Jawdat Clinical Neurophysiology 132 (1), 94-103, 2021 | 6 | 2021 |
Safety and efficacy of arimoclomol for inclusion body myositis: a multicentre, randomised, double-blind, placebo-controlled trial PM Machado, MP McDermott, T Blaettler, C Sundgreen, AA Amato, ... The Lancet Neurology 22 (10), 900-911, 2023 | 5 | 2023 |
Preface: promoting research in PLS: current knowledge and future challenges H Mitsumoto, MR Turner, all Delegates of the PLS Conference, ... Amyotrophic lateral sclerosis and frontotemporal degeneration 21 (sup1), 1-2, 2020 | 5 | 2020 |
Design and Statistical Innovations in a Platform Trial for Amyotrophic Lateral Sclerosis M Quintana, BR Saville, M Vestrucci, MA Detry, L Chibnik, J Shefner, ... Annals of Neurology 94 (3), 547-560, 2023 | 4 | 2023 |